The USFDA's Office of Orphan Drug Products grants orphan status to support development of medicines for the treatment of rare diseases that affect fewer than 200,000 people in the US. “This Orphan ...

However, “orphan drugs” provide hope by offering treatment options that improve their quality of life and potentially extend life expectancy. “Orphan” diseases affect small patient ...

As a young girl in the 1990s, I was surrounded by orphan stories: our family’s creaky VHS tape of the 1982 version of “Annie”; the well-thumbed library paperbacks of “The Boxcar Children ...