Solid Biosciences: Differentiating Factors Of SGT-212 To Set Itself Apart
Initiation of Phase 1b study using SGT-212 for the treatment of patients with Friedreich's Ataxia expected in 2H25. Click ...
Muscular Dystrophy News19h
Corticosteroid at low dose may help with muscle damage, inflammation
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...
Whitecourt Star21h
Photos: Whitecourt Wolverines fans save the day at 2025 Superhero Night, support non-profits
Dillon, left, as Supergirl, Dominique Dickson as Wonder Mom and Dason as Raphael the Ninja Turtle got into the spirit of ...
Solid Biosciences Receives FDA Fast Track Designation for SGT-212 Dual Route of Administration Gene Therapy for Friedreich’s Ataxia
Only dual route gene transfer therapy in development to treat Friedreich’s ataxia with FDA IND clearance and Fast Track designation - CHARLESTOWN, Mass., Jan. 21, 2025 (GLOBE NEWSWIRE) -- Solid ...
Dyne Therapeutics Receives FDA Fast Track Designation for DYNE-101 for the Treatment of Myotonic Dystrophy Type 1
Company Anticipates Submitting for U.S. Accelerated Approval in H1 2026 -WALTHAM, Mass., Jan. 21, 2025 (GLOBE NEWSWIRE) -- Dyne Therapeutics, ...
Catalyst Pharmaceuticals Posts Corporate Presentation in Recent 8-K Filing
Catalyst Pharmaceuticals, Inc. (NASDAQ: CPRX) recently disclosed in an 8-K filing with the Securities and Exchange Commission on January 13, 2025, that the company has posted a corporate presentation ...
BioSpace1d
2025 Investment to Swing Toward I&I, Obesity, More: Experts
As the year gets underway, analysts and biotech executives highlight cell therapy’s pivot from oncology to autoimmune ...
Le Lézard1d
Defeat Duchenne Canada Marks 30 Years of Progress with Major Research Funding Announcement
Defeat Duchenne Canada is proud to celebrate its 30th anniversary, marking three decades of relentless progress in the fight ...
Struggling With Muscle Weakness? It May Be A Sign Of Muscular Dystrophy
Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early ...
Family of Birmingham girl with one in 50 million condition say 'we want to do everything that we can'
Matilda Baptiste is 16 from Hall Green needs help to buy vital equipment to help her live independently with Duchenne ...
Jackson Lab expanding to Florida. What to know.
The company says it has in total “nearly 3,000 people at 11 locations in Maine, Connecticut, California, Japan and China, and ...